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Clinical Trial
Study Details
Status
RECRUITING
Study ID #
NCT07223203
Study Start
Primary Completion
Study Completion
Enrollment
125
Study Type
Interventional
Phase
Phase 3
Summary

The purpose of this study is to:

* Determine the efficacy of nucresiran in patients with hATTR-PN by evaluating the effect on neurologic impairment, quality of life, nutritional status, disability, and gait speed
* Demonstrate superiority of nucresiran compared to in-study vutrisiran with respect to serum transthyretin (TTR) levels

Conditions
Hereditary Transthyretin-Mediated Amyloidosis With Polyneuropathy
hATTR-PN
Study Contact
Name
Clinical Trial Information Line
Role
Contact
Phone
1-877-ALNYLAM
Email
clinicaltrials@alnylam.com
Name
Clinical Trial Information Line
Role
Contact
Phone
1-877-256-9526
Email
clinicaltrials@alnylam.com
Locations
Facility

Clinical Trial Site
Aurora, Colorado 80045
United States

Facility

Clinical Trial Site
Chicago, Illinois 60611
United States

Facility

Clinical Trial Site
Baltimore, Maryland 21287
United States

Facility

Clinical Trial Site
Boston, Massachusetts 02118
United States

Facility

Clinical Trial Site
Rochester, Minnesota 55905
United States

Facility

Clinical Trial Site
New York, New York 10016
United States

Facility

Clinical Trial Site
New York, New York 10032
United States

Facility

Clinical Trial Site
Chapel Hill, North Carolina 27514
United States

Facility

Clinical Trial Site
Nashville, Tennessee 37232
United States

Facility

Clinical Trial Site
Dallas, Texas 75246
United States

Facility

Clinical Trial Site
Houston, Texas 77030
United States

Facility

Clinical Trial Site
CP2000 Rosario
Argentina

Facility

Clinical Trial Site
Darlinghurst 2010
Australia

Facility

Clinical Trial Site
Woolloongabba 4102
Australia

Facility

Clinical Trial Site
Ribeirão Preto
14051-140
Brazil

Facility

Clinical Trial Site
Rio de Janeiro
22640-100
Brazil

Facility

Clinical Trial Site
São Paulo
04038-002
Brazil

Facility

Clinical Trial Site
Vancouver V5Z 1M9
Canada

Facility

Clinical Trial Site
2371 Égkomi
Cyprus

Facility

Clinical Trial Site
94000 Créteil
France

Facility

Clinical Trial Site
94270 Le Kremlin-Bicêtre
France

Facility

Clinical Trial Site
13005 Marseille
France

Facility

Clinical Trial Site
10117 Berlin
Germany

Facility

Clinical Trial Site
69120 Heidelberg
Germany

Facility

Clinical Trial Site
48149 Münster
Germany

Facility

Clinical Trial Site
115 28 Athens
Greece

Facility

Clinical Trial Site
715 00 Heraklion
Greece

Facility

Clinical Trial Site
Dublin
D24 NR0A
Ireland

Facility

Clinical Trial Site
50134 Florence
Italy

Facility

Clinical Trial Site
20133 Milan
Italy

Facility

Clinical Trial Site
35128 Padova
Italy

Facility

Clinical Trial Site
27100 Pavia
Italy

Facility

Clinical Trial Site
00168 Roma
Italy

Facility

Clinical Trial Site
Bunkyo C
113-8519
Japan

Facility

Clinical Trial Site
Kumamoto
860-8556
Japan

Facility

Clinical Trial Site
Matsumoto-shi
390-8621
Japan

Facility

Clinical Trial Site
Suita
565-0871
Japan

Facility

Clinical Trial Site
59100 Kuala Lumpur
Malaysia

Facility

Clinical Trial Site
1649-035 Lisbon
Portugal

Facility

Clinical Trial Site
4099-001 Porto
Portugal

Facility

Clinical Trial Site
Seoul
05030
South Korea

Facility

Clinical Trial Site
Seoul
06351
South Korea

Facility

Clinical Trial Site
08035 Barcelona
Spain

Facility

Clinical Trial Site
21005 Huelva
Spain

Facility

Clinical Trial Site
8907 L'Hospitalet de Llobregat
Spain

Facility

Clinical Trial Site
28040 Madrid
Spain

Facility

Clinical Trial Site
07198 Palma de Mallorca
Spain

Facility

Clinical Trial Site
113 61 Stockholm
Sweden

Facility

Clinical Trial Site
907 37 Umeå
Sweden

Facility

Clinical Trial Site
3010 Bern
Switzerland

Facility

Clinical Trial Site
Taipei, 10002
Taiwan

Facility

Clinical Trial Site
Taipei, 112
Taiwan

Facility

Clinical Trial Site
Taoyuan City, 33305
Taiwan

Facility

Clinical Trial Site
London
NW3 2QG
United Kingdom

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