Clinical Trial
Study Details
Status
RECRUITING
Study ID #
NCT05250973
Study Start
Primary Completion
Study Completion
Enrollment
150
Study Type
Interventional
Phase
Phase 2
Interventions
Dexamethasone

Dexamethasone will be administered orally or IV.

Primary Outcomes
Measure
Number of Participants with Cardiac Events of Any Toxicity Grade
Description

Number of participants with cardiac events of any toxicity grade will be reported.

Timeframe
Up to 12 months
Measure
Observed Concentration Immediately Prior to the Next Study Treatment Administration (Ctrough) of Daratumumab
Description

Ctrough is defined as the observed concentration immediately prior to the next study treatment administration.

Timeframe
Cycle 3 Day 1 predose (each cycle is of 28 days)
Secondary Outcomes
Measure
Overall Complete Hematologic Response (HemCR) Rate
Description

Overall HemCR rate is defined as percentage of participants who achieve HemCR during or after the study treatment.

Timeframe
Up to Cycle 12 or Month 12 (whichever occurs later)
Measure
HemCR Rate
Description

HemCR rate at 6 month is defined as percentage of participants who achieve HemCR at 6 month during or after the study treatment.

Timeframe
At 6 months
Measure
Very Good Partial Response (VGPR) or Better Rate
Description

Hematologic greater than or equal to (\>=) VGPR rate is defined as percentage of participants who achieve hematologic response of VGPR or better.

Timeframe
Up to Cycle 12 or Month 12 (whichever occurs later)
Measure
Time to HemCR or (VGPR or Better)
Description

For participants who achieve HemCR (or \>=VGPR), time to HemCR (or \>=VGPR) is defined as the time between the date of first study treatment and the first efficacy evaluation at which the participant has met all criteria for hematologic complete response (CR) (or \>=VGPR).

Timeframe
Up to Cycle 12 or Month 12 (whichever occurs later)
Measure
Duration of Response (HemCR and VGPR or Better)
Description

For participants who achieve HemCR (or \>=VGPR), duration of HemCR (or \>=VGPR) is defined as the time between the date of initial documentation of HemCR (or \>=VGPR) to the date of first documented evidence of hematologic progressive disease or death, whichever comes first.

Timeframe
Up to Cycle 12 or Month 12 (whichever occurs later)
Measure
Organ Response Rate (OrRR)
Description

Organ response rate is defined as the percentage of participants who achieve organ response in each corresponding organ (kidney, heart, liver).

Timeframe
Up to Cycle 12 or Month 12 (whichever occurs later)
Measure
Overall Survival (OS)
Description

OS is measured from the date of first study treatment to the date of the participant's death.

Timeframe
Until Cycle 12 or Month 12 (whichever occurs later)
Measure
Time to Subsequent Therapy
Description

Time to subsequent therapy for amyloid light chain (AL) amyloidosis is defined as the time from the date of first study treatment to the start date of subsequent AL amyloidosis (non-protocol) treatment.

Timeframe
Up to Cycle 12 or Month 12 (whichever occurs later)
Measure
Number of Participants with Adverse Events (AEs) by Severity
Description

Number of participants with AEs by severity will be reported. An AE is any untoward medical occurrence in a participant participating in a clinical study that does not necessarily have a causal relationship with the pharmaceutical/ biological agent under study.

Timeframe
Up to Cycle 12 or Month 12 (whichever occurs later)
Measure
Serum Concentration of Daratumumab
Description

Serum samples will be analyzed to determine concentrations of daratumumab.

Timeframe
Up to 3 years
Measure
Number of Participants with Antibodies to Daratumumab
Description

Number of participants with antibodies to daratumumab will be reported.

Timeframe
Up to Cycle 12 or Month 12 (whichever occurs later)
Measure
Number of Participants with Antibodies to Recombinant Human Hyaluronidase PH20 Enzyme (rHuPH20)
Description

Number of participants with antibodies to rHuPH20 will be reported.

Timeframe
Up to Cycle 12 or Month 12 (whichever occurs later)
Measure
Change from Baseline in Clinical Signs and Symptoms Score of Cardiac AL Amyloidosis
Description

Change from baseline in clinical signs and symptoms score of cardiac AL amyloidosis will be reported.

Timeframe
Up to Cycle 12 or Month 12 (whichever occurs later)
Summary

The purpose of this study is to characterize cardiac safety of Daratumumab, Cyclophosphamide, Bortezomib, and Dexamethasone (D-VCd) treatment regimens (Arm A: daratumumab + immediate VCd treatment and Arm B: daratumumab + deferred VCd) in newly diagnosed systemic amyloid light chain (AL) amyloidosis with cardiac involvement and to identify potential mitigation strategies for cardiac toxicity (cohort 1); to characterize the pharmacokinetics of subcutaneous (SC) daratumumab, among racial and ethnic minorities, including Black or African American, with newly diagnosed AL amyloidosis treated with D-VCd (cohort 2).

Conditions
Amyloidosis
Study Contact
Name
Study Contact
Role
Contact
Phone
844-434-4210
Email
Participate-In-This-Study@its.jnj.com
Locations
Facility

City of Hope
Duarte, CA 91010
United States

Facility

Smilow Cancer Hospital/Yale Cancer Center
New Haven, CT 06510
United States

Facility

Moffitt Cancer Center
Tampa, FL 33612
United States

Facility

Winship Cancer Institute Emory University
Atlanta, GA 30322
United States

Facility

Tufts Medical Center
Boston, MA 02111
United States

Facility

Boston University Medical Center
Boston, MA 02118
United States

Facility

Barbara Ann Karmanos Cancer Institute
Detroit, MI 48201
United States

Facility

Memorial Sloan Kettering
New York, NY 10021
United States

Facility

Levine Cancer Institute
Charlotte, NC 28204
United States

Facility

University Hospital of Cleveland
Cleveland, OH 44106
United States

Facility

Ohio Health Research Institute
Columbus, OH 43214
United States

Facility

West Penn Hospital
Pittsburgh, PA 15224
United States

Facility

UT Southwestern Medical Center
Dallas, TX 75390
United States

Facility

VCU Medical Center
Richmond, VA 23219
United States

Facility

University of Washington
Seattle, WA 90805
United States

Facility

Tom Baker Cancer Center
Calgary AB T2N 4N2
Canada

Facility

Cross Cancer Institute
Edmonton AB T6G 1Z2
Canada

Facility

University Health Network (UHN) Princess Margaret Cancer Centre
Toronto ON M5G 2M9
Canada

Facility

Peking University First Hospital
Beijing
100034
China

Facility

Peking University People s Hospital
Beijing
100044
China

Facility

West China Hospital Si Chuan University
Chengdu
610041
China

Facility

First affiliated Hospital of Zhejiang University
Hangzhou
310020
China

Facility

Ruijin Hospital, Shanghai Jiao Tong University
Shanghai
200025
China

Facility

CHU de Limoges
87042 Limoges Cedex
France

Facility

Centre hospitalier Lyon-Sud
69495 Pierre Benite cedex
France

Facility

CHU De Poitiers
86000 Poitiers
France

Facility

CHU Rangueil
31400 Toulouse
France

Facility

Charite Campus Benjamin Franklin
12203 Berlin
Germany

Facility

Universitatsklinikum Essen
45122 Essen
Germany

Facility

Universitaetsklinikum Heidelberg Medizinische Klinik V
69120 Heidelberg
Germany

Facility

Alexandra General Hospital of Athens
11528 Athens
Greece

Facility

Università Degli Studi Di Napoli Federico Ii
80131 Napoli
Italy

Facility

Fondazione IRCCS Policlinico San Matteo
27100 Pavia
Italy

Facility

DIPARTIMENTO DI BIOTECNOLOGIE CELLULARI ED EMATOLOGIA - UNIVERSITà ''LA SAPIENZA''
00161 Roma
Italy

Facility

University Medical Center Groningen
9713 GZ Groningen
Netherlands

Facility

Hospital Maastricht University Medical Center
6229 HX Maastricht
Netherlands

Facility

UMC Utrecht
3584 CX Utrecht
Netherlands

Facility

Hosp. Univ. Germans Trias I Pujol
08916 Badalona
Spain

Facility

Hosp. Univ. Vall D Hebron
08035 Barcelona
Spain

Facility

Hosp. Clinic de Barcelona
08036 Barcelona
Spain

Facility

Clinica Univ. de Navarra
28027 Madrid
Spain

Facility

Clinica Univ. de Navarra
31008 Pamplona
Spain

Facility

Hosp. Clinico Univ. de Salamanca
37007 Salamanca
Spain

Facility

Leicester Royal Infirmary - Haematology
Leicester
LE1 5WW
United Kingdom

Facility

University College Hospital
London
NW1 2PG
United Kingdom

Eligibility Criteria

Inclusion Criteria:

* Cohort 1: Cardiac involvement (amyloid light chain \[AL\] amyloidosis Mayo Cardiac Stage II and Stage IIIa) with or without other organ(s) involved; Cohort 2: One or more organs impacted by systemic AL amyloidosis according to consensus guidelines
* Eastern Cooperative Oncology Group (ECOG) Performance Status score of 0, 1 or 2
* A female participant of childbearing potential must have a negative serum or urine test at screening and within 72 hours of the first dose of study treatment and must agree to further serum or urine pregnancy tests during the study
* A male participant must agree not to donate sperm for the purpose of reproduction during the study and for a minimum of 6 months after receiving the last dose of cyclophosphamide or 100 days after discontinuation of daratumumab, whichever is longer
* Cohort 2 only: self-identified racial and ethnic minorities, including Black or African American
* Measurable disease at screening defined by one of the following:

Difference between iFLC and uninvolved FLC (dFLC) \>= 40mg/L per central laboratory Serum involved free light chain (iFLC) \>= 40 mg/L with an abnormal kappa:lambda ratio Serum M-protein \>= 0.5 g/dL

Exclusion Criteria:

* Prior therapy for systemic AL amyloidosis or multiple myeloma including medications that target cluster of differentiation 38 (CD38), with the exception of 160 milligrams(mg) dexamethasone or equivalent corticosteroid maximum exposure prior to randomization/enrollment
* Previous or current diagnosis of symptomatic multiple myeloma, including the presence of lytic bone disease, plasmacytomas, \>=60% plasma cells in the bone marrow, or hypercalcemia related to myeloma.
* Participant received any of the following therapies:

1. treatment with an investigational drug or used an invasive investigational medical device within 14 days or at least 5 half-lives, whichever is less;
2. vaccinated with an investigational vaccine (except for COVID-19) live, attenuated or replicating viral vector vaccines less than (\<) 4 weeks prior to randomization/enrollment. Participants who are taking strong Cytochrome P450 3A4(CYP3A4) inducers must discontinue their use at least 5 half-lives prior to the first dose of bortezomib
* Stem cell transplantation -Planned stem cell transplant during the first 9 cycles of protocol therapy are excluded. Stem cell collection during the first 9 cycles of protocol therapy is permitted
* Grade 2 sensory or Grade 1 painful peripheral neuropathy

Eligibility Minimum Age
18 Years
Sexes Eligible for Study
ALL
Eligibility Std Ages
Adult
Older Adult